Joint with: Precision Genome Engineering: From Laboratory to Clinic
Targeted Delivery of Nucleic Acid Medicines

Jan 01–04, 2027 | Location to be Determined
Scientific Organizers: C. Frank Bennett, Beverly L. Davidson, and Daniel G. Anderson

  In Person
  On Demand
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Jan 01–04, 2027 | Location to be Determined

Scientific Organizers: C. Frank Bennett, Beverly L. Davidson, and Daniel G. Anderson

Supported by the  Directors' Fund

***Meeting program subject to change.

Available Formats:   = In Person     = On Demand
Friday, January 1, 2027
Registration
4:00–8:00 PM
Welcome Mixer
6:00–8:00 PM
Saturday, January 2, 2027
Breakfast
7:00–8:00 AM
Welcome and Keynote Address (Joint)
8:00–9:00 AM
Eric N. Olson †, University of Texas Southwestern Medical Center
Single-AAV base Editing Therapies for Duchenne Muscular Dystrophy
Viral Delivery of Genome Editors and Genetic Medicines (Joint)
9:00–11:15 AM
Beverly L. Davidson, Children’s Hospital of Philadelphia and University of Pennsylvania
AAV Capsid Engineering for Broad CNS Distribution
Sonia Vallabh †, Broad Institute
Development of Medicines to Treat Prion Diseases: A Personal Journey
Charles Gersbach †, Duke University
AAV-Delivered Epigenome Editors
Short Talk(s) Chosen from Abstracts
Coffee Break
9:30–9:50 AM
Poster Setup
11:15–1:00 PM
On Own for Lunch
11:15–5:00 PM
Poster Viewing
1:00–10:00 PM
Symposia Spotlight 1: Late-breaking research presentations selected from abstract submissions
2:30–4:30 PM
Short Talks Chosen from Abstracts
Coffee Available
4:30–5:00 PM
Tissue Targeting of LNPs
5:00–7:00 PM
Daniel G. Anderson, Massachusetts Institute of Technology
LNP Delivery of Nucleic Acid Medicines
Jessica A. Couch †, ReCode Therapeutics
LNP Delivery with the CNS
Kathryn Whitehead †, Carnegie Mellon University
Optimizing LNPs Delivery Vehicles
Short Talk(s) Chosen from Abstracts
Social Hour with Dinner
7:00–8:00 PM
Posters
7:30–10:00 PM
Sunday, January 3, 2027
Breakfast
7:00–8:00 AM
Keynote Address (Joint)
8:00–9:00 AM
David R. Liu †, Broad Institute, HHMI, and Harvard University
Development and Application of Virus-Like Particles for Genome Editing in vivo
Coffee Break
9:00–9:20 AM
In vivo Genome Editing via Non-Viral Delivery (Joint)
9:00–11:00 AM
Birgit C. Schultes †, IntelliaTherapeutics Inc.
Clinical Results from Liver Genome Editing in vivo
Rebecca Ahrens-Nicklas †, Children's Hospital of Philadelphia
Personalized Therapeutic Genome Editing for Hepatic Inborn Errors of Metabolism
Leah R. Sabin †, Regeneron Pharmaceuticals
Novel Delivery Strategies for Genetic Medicines
Short Talk(s) Chosen from Abstracts
Poster Setup
11:00–1:00 PM
On Own for Lunch
11:00–5:00 PM
Poster Viewing
1:00–10:00 PM
Career Roundtable
3:00–4:30 PM
Coffee Available
4:30–5:00 PM
Ligand Mediated Delivery of Nucleic Acid Medicines
5:00–7:00 PM
Deborah Law †, Xaira Therapeutics
Machine Learning Design of Ligands for Targeted Delivery of Nucleic Acid Medicines
Vadim Dudkin †, Souffle Therapeutics
Targeted Delivery of Genetic Medicines
C. Frank Bennett, Ionis Pharmaceuticals, Inc.
Targeted Delivery of Oligonucleotide Drugs
Short Talk(s) Chosen from Abstracts
Social Hour with Dinner
7:00–8:00 PM
Posters
7:30–10:00 PM
Monday, January 4, 2027
Breakfast
7:00–8:00 AM
Translation of Genetic Medicines to the Clinic
8:00–11:00 AM
Joseph B. Bolen †, Orna Therapeutics
Tissue Selective Delivery of Circular RNAs
Christian Mueller †, Sanofi
Genome Editing in vivo via Non-Viral Delivery Platforms
Dirk Grimm †, University of Heidelberg
AAV Capsid Engineering
Nicole K. Paulk †, UCSF
AAV Delivery to Cancer Cells
Short Talk(s) Chosen from Abstracts
Coffee Break
9:00–9:20 AM
On Own for Lunch
11:00–5:00 PM
Symposia Spotlight 2: Late-breaking research presentations selected from abstract submissions
2:30–4:30 PM
Short Talks Chosen from Abstracts
Coffee Available
4:30–5:00 PM
New Delivery Technologies
5:00–6:45 PM
Dong-Jiunn Jeffery Truong †, Helmholtz Munich
VLP Deliver of cas Enzymes
Akin Akinc †, Alnylam Pharmaceuticals Inc.
Use of Endogenous Retroviral Capsid for Delivery of Nucleic Acid Medicines
Bowen Li †, University of Toronto
Machine Learning Design of LNP Delivery Systems
Short Talk(s) Chosen from Abstracts
Meeting Wrap-Up: Outcomes and Future Directions (Organizers)
6:45–7:00 PM
Social Hour with Dinner
7:00–8:00 PM
Entertainment
8:00–11:00 PM
Cash Bar
8:00–11:00 PM
Tuesday, January 5, 2027
Departure
12:00–11:59 PM

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